FDA grants Orphan Drug Designation for AJ1-11095 for the Treatment of Myelofibrosis
“Orphan Drug Designation is an important milestone in our clinical development of AJ1-11095 for the treatment of myelofibrosis,” said David Steensma, MD, FACP, Chief Medical Officer of Ajax. “This designation reinforces the compelling need for effective new treatment options for patients suffering from myelofibrosis, and supports our continued efforts to advance AJ1-11095 to address the unmet need for patients who would benefit from improved treatment efficacy, or who have not responded to existing therapies.”
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