FDA Orphan Drug Designation for HT-KIT in Rare c-KIT-Driven Cancers
“HT-KIT’s transcript-level suppression of KIT has now produced consistent anti-tumor performance across models, with a clean preclinical tolerability profile and GLP-ready analytics,” said Robb Knie, Chief Executive Officer. “With Orphan Drug Designation secured and an IND-enabling package progressing, we are preparing for a disciplined entry into first-in-human evaluation.”
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